Regulatory & Policy

Japan approves Brinsupri as first treatment for non-cystic fibrosis bronchiectasis

Japan approves Brinsupri as first treatment for non-cystic fibrosis bronchiectasis

Japan's Ministry of Health, Labour and Welfare (MHLW) has approved Brinsupri (brensocatib) for non-cystic fibrosis bronchiectasis (NCFB) in adults and pediatric patients aged 12 years and older, making it the first approved treatment for the condition in Japan. Bridgewater, New Jersey-based Insmed Incorporated (Nasdaq: INSM) now holds approvals in the US, EU, and Japan for the oral, once-daily dipeptidyl peptidase 1 (DPP1) inhibitor, which received US FDA approval in August 2025 as the first therapy specifically indicated for NCFB.

The Japan approval covers brensocatib 25 mg tablets taken once daily, with no additional biomarker or exacerbation-history qualifier — a broader label than the EU and UK, where approval requires at least two exacerbations in the prior 12 months. Brensocatib acts by reversibly inhibiting DPP1, a lysosomal cysteine protease that activates neutrophil serine proteases during neutrophil maturation in the bone marrow; blocking this upstream step reduces chronic neutrophilic airway inflammation without directly depleting circulating neutrophils.

The MHLW decision is based on the Phase III ASPEN study, in which brensocatib 25 mg significantly reduced pulmonary exacerbation rates versus placebo over 52 weeks, prolonged time to first exacerbation, and increased the proportion of patients remaining exacerbation-free. Patients on the 25 mg dose also showed significantly lower lung function decline at week 52, measured by post-bronchodilator forced expiratory volume in one second (FEV1). The most common treatment-emergent adverse events occurring in at least 5% of patients were COVID-19, nasopharyngitis, cough, and headache.

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The news provides a boost to Insmed after development of brensocatib in hidradenitis suppurativa was discontinued after the CEDAR study failed to meet its primary endpoint.

Brinsupri remains the only approved treatment specifically indicated for NCFB in the US, EU, and Japan. In the pipeline, AstraZeneca's tozorakimab, an anti-interleukin-33 monoclonal antibody that met its primary endpoint in Phase III chronic obstructive pulmonary disease exacerbation trials, has been cited by AstraZeneca management as a candidate for bronchiectasis development. AstraZeneca also tested benralizumab (Fasenra) in the eosinophilic NCFB subpopulation in the Phase III MAHALE trial, but failed to meet the primary endpoint, removing a leading biologic challenger from the near-term competitive field.


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