Regulatory & Policy

ArriVent moving MUC16/NaPi2b-targeted ADC into trials against ovarian and endometrial cancers

ArriVent BioPharma (Nasdaq: AVBP), based in Newtown Square, Pennsylvania, announced IND clearance from the US FDA for ARR-002, a dual-target tetravalent antibody-drug conjugate directed against MUC16 and NaPi2b, with an initial clinical focus in ovarian and endometrial cancers. The company said it expects to initiate a Phase I trial and dose the first patient in the second half of 2026.

ARR-002, also designated AV-P138-ADC, is designed as a tetravalent construct in a 2+2 bispecific format, simultaneously engaging both MUC16 — widely known as CA-125 — and NaPi2b, a sodium-dependent phosphate transporter encoded by SLC34A2. Both antigens are reported to be highly expressed on ovarian and endometrial tumor cells with limited expression in normal tissues. The molecule uses site-specific conjugation to vcMMAE at a drug-to-antibody ratio of 4, a design intended to deliver a homogeneous, stable construct with controlled payload release following internalization.

The scientific rationale centers on limitations observed with single-target ADCs. Heterogeneous antigen expression across tumor cells is a recognized mechanism of resistance or incomplete response for agents that rely on a single surface marker. By engaging two targets simultaneously, ARR-002 is designed to increase avidity, improve internalization efficiency, and reduce the probability of tumor escape through downregulation of either target alone. ArriVent said preclinical data presented at the 2026 American Association for Cancer Research Annual Meeting — in a joint presentation with Aarvik Therapeutics, the company's collaborator on the construct — demonstrated effective simultaneous engagement of both targets, enhanced internalization relative to single-target antibody controls, and superior in vivo efficacy versus single-target ADCs in the OVCAR-3 xenograft model. A tolerability assessment in cynomolgus monkeys showed reversible hematologic findings at a higher maximum tolerated single dose compared to other approaches in development, which the company characterized as a potentially wider therapeutic window, though cross-species extrapolation carries inherent limitations.

The ADC landscape for ovarian cancer

The ovarian cancer ADC field has a defined benchmark in mirvetuximab soravtansine (Elahere), developed by ImmunoGen and now marketed by AbbVie following its acquisition. Mirvetuximab targets folate receptor alpha and received full US FDA approval in March 2024 for platinum-resistant ovarian cancer with high FRα expression. It represents the first and currently only approved ADC in this setting, but its eligibility is constrained by the FRα biomarker threshold, leaving a substantial proportion of patients — those with low or absent FRα expression — without a targeted ADC option.

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ARR-002's MUC16/NaPi2b targeting addresses a different antigen pair, one with potentially broader expression across the ovarian cancer population. MUC16 is the antigen underlying CA-125, a marker used clinically for disease monitoring, and its surface expression on ovarian tumors is well established. NaPi2b has been investigated as a target in ovarian cancer for over a decade, most notably by Genentech, which developed lifastuzumab vedotin, a NaPi2b-targeting ADC that progressed into Phase II evaluation before development was discontinued. That prior clinical experience with NaPi2b as a single target provides some validation of the antigen's relevance in this tumor type, even as it underscores the challenge of achieving sufficient efficacy through single-target engagement alone — a limitation that ARR-002's dual-target design is explicitly intended to address.

The ARR-002 IND clearance places ArriVent in a competitive but still relatively open field for dual-target ADCs in gynecologic oncology. While bispecific ADC formats are an active area of industry research, few have reached clinical evaluation with this specific antigen combination, and none targeting MUC16 and NaPi2b simultaneously have disclosed clinical data.


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