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Cerevance closes USD 20 million Series C as Phase III Parkinson's trial reaches full enrollment

Cerevance's Phase III Parkinson's trial reaches full enrollment as USD 20 million Series C extends runway

Boston-based Cerevance has completed enrollment in its pivotal Phase III ARISE trial of solengepras in Parkinson's disease and closed an oversubscribed USD 20 million Series C financing round, positioning the company for a topline data readout by end of Q3 2026.

The Series C was funded entirely by existing investors, with participation from Double Point Ventures, Gates Frontier, Google Ventures, Lightstone Ventures, MQB Partners, SV Health Investors' Dementia Discovery Fund, and UPMC. No new investors joined the round. Proceeds are intended to fund operations into mid-2027, covering the completion of ARISE and continued pipeline advancement. The round follows a USD 47 million Series B-1 extension closed in April 2024, which was itself part of a cumulative Series B-1 raise totaling USD 98 million. Total financing raised by the company now exceeds USD 180 million across all rounds since its 2016 founding.

The ARISE trial and what it is measuring

The Phase III ARISE trial is a multicenter, randomized, double-blind, placebo-controlled study evaluating solengepras as an adjunctive therapy to levodopa and other standard-of-care Parkinson's medications. The trial enrolled 341 patients aged 30 and older across sites in the US, Europe, the United Kingdom, and Australia. Eligible patients were required to experience an average of three or more hours of total OFF time per day — the periods during which Parkinson's symptoms recur or worsen despite ongoing medication.

Participants were randomized to receive solengepras at 75 mg or 150 mg, or placebo, administered once daily for 12 weeks. The primary endpoint is the change from baseline to week 12 in average daily OFF time for the 150 mg dose versus placebo. Secondary objectives include assessments of safety and tolerability, ON time, non-motor symptoms including daytime sleepiness, cognitive function, and quality-of-life measures using the Movement Disorder Society-UPDRS and PD Questionnaire 39, among others.

The mechanism behind solengepras

Solengepras — also known as CVN424 — is a selective oral inverse agonist of the GPR6 receptor, a target expressed in striatal indirect pathway neurons. Its mechanism is distinct from all approved Parkinson's therapies in that it does not act on the dopamine system. Current standard-of-care treatments, including levodopa, work by replenishing or mimicking dopamine. While effective in early disease, these approaches are associated with motor fluctuations and dyskinesias over time as their therapeutic window narrows.

By targeting GPR6 in the indirect basal ganglia pathway, solengepras is designed to modulate motor circuit activity without directly altering dopamine signaling. The company said this approach may reduce OFF periods while carrying a lower risk of the side effects typically associated with long-term dopaminergic therapy. Phase II data published in 2024 in EClinicalMedicine reported reductions in OFF time and a favorable tolerability profile, providing the clinical rationale for the Phase III program.

The NETSseq platform and its academic origins

Cerevance's pipeline is built on a proprietary drug discovery platform called NETSseq — Nuclear Enriched Transcript Sort sequencing — which was developed by Nathaniel Heintz and Xiao Xu during postdoctoral research at The Rockefeller University. Cerevance was co-founded by Heintz and Xu in 2016 and licensed the technology from Rockefeller at the time of the company's formation.

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The platform addresses a longstanding limitation in CNS drug discovery: the inability to study human brain tissue at the resolution of individual cell types. NETSseq works by isolating nuclei — rather than whole cells — from post-mortem human brain samples, sorting them by cell type using fluorescence-activated methods, and then performing deep transcriptomic sequencing on each isolated population. Because nuclei are more stable than whole cells in post-mortem tissue, the approach enables analysis of large collections of aged and diseased human brain samples that would otherwise be inaccessible to standard single-cell techniques.

The scientific rationale is that bulk tissue analysis — which averages gene expression across all cell types simultaneously — masks the cell-type-specific molecular signals that drive neurological disease. By resolving those signals at the level of individual neuronal and glial populations, NETSseq can identify targets that are selectively expressed in the specific cell types affected by a given disease. This selectivity is both a discovery advantage and a potential therapeutic one: drugs acting on highly cell-type-specific targets may carry a reduced risk of off-target effects.

GPR6, the target of solengepras, was identified through this approach as being selectively expressed in striatal indirect pathway neurons — the circuit implicated in Parkinson's motor control. The company's second pipeline candidate, CVN293, was similarly derived from NETSseq analysis and targets THIK1 (KCNK13), a two-pore potassium channel expressed in microglia. CVN293 is positioned for potential application in neurodegenerative disorders and obesity, though no clinical trial registration for that program has been publicly disclosed.

Cerevance also holds a research collaboration with Merck & Co. focused on identifying novel targets for Alzheimer's disease using the NETSseq platform. That deal, announced in August 2022, carries potential milestone and royalty payments of up to approximately USD 1.1 billion, and the company has publicly reported achieving at least two milestones under the agreement.

The company operates from dual locations: its corporate headquarters in Boston, Massachusetts, and a research base at Cambridge Science Park in the United Kingdom, where it was originally incorporated in 2016 as Cerevance Ltd. Chief executive Craig Thompson has said the company is "well positioned from both a clinical and financial standpoint" ahead of the Q3 2026 topline readout.


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