Regulatory & Policy

FDA grants priority review to Jazz Pharmaceuticals' Ziihera for first-line HER2-positive gastric cancer

Jazz Pharmaceuticals submitted a supplemental Biologics License Application (sBLA) to the US FDA for Ziihera (zanidatamab-hrii) in combination regimens for the first-line treatment of adults with HER2-positive unresectable locally advanced or metastatic gastric, gastroesophageal junction, or gastroesophageal adenocarcinoma. The FDA accepted the filing and granted Priority Review, with a PDUFA target action date of August 25, 2026.

The sBLA is being reviewed under the FDA's Real-Time Oncology Review program. The filing covers zanidatamab-hrii in combination with fluoropyrimidine- and platinum-containing chemotherapy, with or without the PD-1 inhibitor Tevimbra (tislelizumab), a product of BeOne Medicines. The FDA had previously granted Breakthrough Therapy designation to zanidatamab for this combination approach in first-line HER2-positive advanced gastric and esophageal adenocarcinoma, the company said.

The application is supported by data from the HERIZON-GEA-01 trial, a global, randomized, open-label Phase III study conducted jointly with BeOne Medicines. The trial enrolled 914 patients across approximately 300 sites in more than 30 countries, randomizing participants to one of three arms: zanidatamab plus chemotherapy and tislelizumab; zanidatamab plus chemotherapy alone; or trastuzumab plus chemotherapy. Eligible patients had unresectable locally advanced, recurrent, or metastatic HER2-positive gastroesophageal adenocarcinoma, defined as HER2 IHC 3+ or IHC 2+ with ISH positivity per central assessment. The trial carries dual primary endpoints of progression-free survival by blinded independent central review and overall survival. Results were presented in January 2026 at the ASCO Gastrointestinal Cancers Symposium.

The HER2-positive gastroesophageal adenocarcinoma space has undergone substantial change since trastuzumab (Herceptin) became the first HER2-directed therapy approved in this setting in 2010, based on the ToGA trial. The current first-line standard for patients with HER2-positive and PD-L1 CPS of 1 or greater is pembrolizumab (Keytruda) combined with trastuzumab and platinum-fluoropyrimidine chemotherapy, following the KEYNOTE-811 Phase III trial. For the subset of patients with CPS below 1, trastuzumab plus chemotherapy remains the standard. Despite these advances, median overall survival in the metastatic setting remains below 20 months, and HER2 heterogeneity and acquired resistance to trastuzumab continue to limit the durability of response.

Zanidatamab-hrii is mechanistically distinct from trastuzumab. As a bispecific antibody, it binds simultaneously to two non-overlapping extracellular domains of HER2, domains II and IV, compared with trastuzumab's single domain IV binding. This dual-epitope engagement is designed to produce more complete receptor blockade, promote HER2 internalization and downregulation, and induce antibody-dependent cellular cytotoxicity, complement-dependent cytotoxicity, and antibody-dependent cellular phagocytosis. The approach is intended to address the limitations of single-epitope HER2 inhibition, including incomplete blockade in tumors with HER2 heterogeneity.

Ziihera already holds US FDA approval in a separate indication: previously treated, unresectable or metastatic HER2-positive biliary tract cancer, where it received accelerated approval based on overall response rate and duration of response. The current sBLA represents the first regulatory submission for zanidatamab-hrii in a gastroesophageal adenocarcinoma setting and, if approved, would position it as the only bispecific HER2-directed antibody in that disease area. Zanidatamab was originally developed by Zymeworks and is being advanced by Jazz Pharmaceuticals and BeOne Medicines under license agreements.

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The HERIZON-GEA-01 trial's three-arm design directly addresses a clinical question that the KEYNOTE-811 data left partially open: whether adding an anti-PD-1 agent to a HER2-directed backbone provides benefit across the full HER2-positive population, including patients with low or absent PD-L1 expression. The pembrolizumab combination was ultimately restricted to PD-L1 CPS of 1 or greater after the CPS below 1 subgroup showed no overall survival benefit. Jazz has noted that the HERIZON-GEA-01 data demonstrated activity across both PD-L1-positive and PD-L1-negative tumors, though detailed subgroup results from the public presentation have not been fully reproduced in the available source materials.

The filing enters a competitive landscape that includes trastuzumab and its biosimilars, pembrolizumab combinations, and fam-trastuzumab deruxtecan-nxki (Enhertu), an antibody-drug conjugate approved in previously treated HER2-positive gastric and gastroesophageal junction adenocarcinoma. Gastroesophageal adenocarcinoma is the fifth most common cancer globally, and approximately 20% of patients have HER2-positive disease, the company said, citing published literature. Five-year survival rates remain below 30% for gastric cancer and approximately 19% for gastroesophageal adenocarcinoma overall.

The Priority Review designation shortens the standard FDA review period from ten months to six months, reflecting the agency's assessment that the drug may offer an advance over available therapy. The PDUFA date of August 25, 2026 sets the timeline for a potential regulatory decision.


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