Discovery

Daraxonrasib study reveals resistance mechanisms in pancreatic cancer

Researchers at Redwood City, California-based Revolution Medicines and Dana-Farber Cancer Institute have published the first systematic characterization of...

Daraxonrasib study reveals resistance mechanisms in pancreatic cancer

Pancreatic cancers treated with daraxonrasib can escape through multiple, often simultaneous routes, according to the first systematic analysis of resistance to Revolution Medicines' multi-selective RAS inhibitor — but the study also identified combination strategies capable of shutting down several of those escape routes in preclinical models. Published August 12 in Nature Medicine, the study, carried out by Revolution Medicines and Dana-Farber Cancer Institute, analyzed tumor evolution in patients with RAS-mutant metastatic PDAC treated with daraxonrasib (RMC-6236), alongside cellular and animal models designed to reproduce and interrogate the resistance mechanisms.

The findings arrive at a pivotal point for daraxonrasib, with Revolution last month beginning an NDA filing after the drug nearly doubled overall survival versus chemotherapy in the Phase III RASolute 302 trial (NCT06577571) in previously treated metastatic PDAC. Understanding how resistance emerges before the drug reaches wider clinical use could give the field an opportunity to design combination regimens prospectively rather than reactively.

Heterogeneous, polyclonal resistance

In the study, circulating tumor DNA (ctDNA) profiling using an 800-plus gene panel from Guardant Health was performed on paired pre- and post-treatment samples from 44 patients with RAS-mutant metastatic PDAC enrolled on the Phase I/II monotherapy trial (NCT05379985). The authors reported that resistance was both heterogeneous and polyclonal — multiple co-occurring mechanisms were detected within individual patients, with no single alteration dominating.

On-target mechanisms, meaning those that reactivate RAS signaling directly, were predominant and included secondary NRAS and HRAS switching mutations and KRAS amplification, identified in approximately 36% of patients. Off-target mechanisms included ERBB2 (HER2) amplification, MET amplification, EGFR alterations, and Hippo/YAP pathway changes. Notably, the researchers detected no secondary KRAS point mutations in the PDAC cohort, contrasting with resistance patterns reported for covalent KRAS G12C inhibitors such as Lumakras (sotorasib) and Krazati (adagrasib). Instead, resistance frequently involved alterations elsewhere in the RAS network or activation of alternative signaling pathways.

Mechanism and preclinical validation

Daraxonrasib works as a molecular glue, recruiting cyclophilin A to active, GTP-bound RAS to form a ternary complex that prevents RAS from engaging downstream effectors. Unlike mutation-selective KRAS inhibitors, it is designed to inhibit active KRAS, NRAS and HRAS across multiple RAS variants.

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Serial in vivo passaging of PDAC cell lines under drug pressure recapitulated the clinically observed resistance alterations, and deep mutational scanning provided a broader landscape of secondary mutations that could confer resistance beyond those seen in the clinical cohort. Resistant lines showed restored pERK and pAKT signaling consistent with clinical observations.

Combinations address specific escape nodes

The researchers then tested whether resistance could be countered by matching combination partners to individual escape mechanisms. Preclinical tests included daraxonrasib combined with Revolution's zoldonrasib (RMC-9805), a KRAS G12D-selective RAS(ON) inhibitor, produced statistically significant superior tumor growth inhibition versus either monotherapy in G12D-mutant models, addressing on-target RAS reactivation. A Phase I/II trial of this doublet (NCT06040541) is already enrolling. For HER2-amplified or HER2-overexpressing models, the combination with trastuzumab deruxtecan (T-DXd, Enhertu) produced tumor regression versus monotherapy controls. Daraxonrasib combined with the EGFR/MET bispecific antibody amivantamab (Rybrevant) demonstrated superior tumor control in receptor tyrosine kinase-driven resistance models. And checkpoint inhibitors targeting WEE1 or CHK1 and TEAD inhibition also showed enhanced activity in models driven by KRAS amplification or Hippo-pathway alterations, respectively.

The findings suggest there may be no single dominant resistance mechanism to target as daraxonrasib moves through late-stage development. Instead, the heterogeneous and often polyclonal escape patterns observed in patients may require biomarker-guided combinations matched to the resistance mechanisms that emerge — an approach Revolution Medicines is already beginning to test clinically.


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